Poswar, F. de O., F. Q. Mayer, M. G. Burin, U. da S. Matte, R. Giugliani, e G. Baldo. “Long-Term Restoration of Alpha-L-Iduronidase Activity in Fibroblasts from Patients With Mucopolysaccharidosis Type I After Non-Viral Gene Transfer”. Clinical and Biomedical Research, vol. 37, nº 4, dezembro de 2017, doi:10.22456/2357-9730.74048.