POSWAR, Fabiano de Oliveira; MAYER, Fabiana Quoos; BURIN, Maira Graeff; MATTE, Ursula da Silveira; GIUGLIANI, Roberto; BALDO, Guilherme. Long-term restoration of alpha-L-iduronidase activity in fibroblasts from patients with mucopolysaccharidosis type I after non-viral gene transfer. Clinical and Biomedical Research, [S. l.], v. 37, n. 4, 2017. DOI: 10.22491/2357-9730.74048. Disponível em: https://seer.ufrgs.br/index.php/hcpa/article/view/74048. Acesso em: 22 ago. 2026.